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Trial Design: Pain Sections
Author Bio
Introduction
Placebo Effects
Single Dose Trials
Repeated Dose Trials
Explanatory Versus Pragmatic
Currently selected section: Dose-Response
Parallel Group Versus Crossover
Conclusion
 

 

Chapter 1: Clinical Trials of Pain Treatment: Dose-Response; Relative Potency; Combinations

 
           

Studies of Analgesic Combinations Single analgesics often fail to relieve more than a portion of the patient’s pain. For example, meta-analyses of randomized trials in neuropathic pain (Sindrup and Jensen, 1999) show that after correction for placebo effects, even the most effective treatments (opioids, tricyclic antidepressants, and gabapentin) only reduce pain by 50% or more in one of every three patients treated. Similar limits encountered treating hypertension, congestive heart failure, cancer, and infectious diseases have been overcome by the use of drug combinations. However, apart from combinations of NSAIDs and acetaminophen with opioids, there have been few clinical trials of analgesic combinations, so this is a major research need.

For basic researchers, studies of drug combinations have become an active topic. Debate on the methodology for analgesic drug combination studies in animals has focused on whether the combination produces synergy for analgesia, defined as an effect that exceeds the sum of the analgesia expected from the components (Berenbaum, 1989). However, from the clinician’s point of view, the emphasis on synergy is misplaced. The key issue regarding clinical usefulness is whether the combination has a better therapeutic ratio (ratio of analgesia to side effects) than either component, or produces a higher maximal analgesic efficacy at tolerable doses. Treatment groups must be chosen to ensure that a comparison of side effects at equianalgesic doses will be possible (Max, 1994). In order to be certain of the ability to compare equal levels of analgesia, at least by interpolation, one needs to study more than one dose of at least one, and optimally each, of the treatment regimens (Carter and Carchman, 1988; Lavigne et al., 1989; Plummer and Short, 1990; Eisenach et al., 1994; Max, 1994; Sethna et al., 1998; Levine et al., 1988). An example of such a design is the relative potency bioassay discussed above (Figure 6.3.1). In order to be clinically useful, the components need not be synergistic for analgesia; they may be merely additive or even subadditive, as long as side effects show even less additivity in the combination.

 

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